Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients

• DOI: 10.1016/j.ymgme.2020.12.127
• Publication Date: 2021-02-01T16:14:15Z
• Authors: Priya S. Kishnani; Shahram Attarian; Joao Lindolfo Borges; Francoise Bouhour; Yin-Hsiu Chien; Young-Chul Choi; Paula Clemens; John Day; Jordi Diaz-Manera; Sevim Erdem-Ozdamar; Ozlem Goker-Alpan; Sergey Illarioshkin; Anna Kostera-Prus...; Hani Kushlaf; Shafeeq Ladha; Tahseen Mozaffar; Mark Roberts; Volker Straub; Antonio Toscano; Ans van der Ploeg; Kristina An Haack; Olivier Huynh-Ba; Tianyue Zhou; Mazen Dimachkie; Benedikt Schoser
• Keywords: 03 medical and health sciences; 0302 clinical medicine