Isaralgagene civaparvovec (ST-920) gene therapy in adults with Fabry disease: Updated results from an ongoing phase 1/2 study (STAAR)

• DOI: 10.1016/j.ymgme.2023.107884
• Publication Date: 2024-01-31T20:41:01Z
• Authors: Robert J. Hopkin; Jaya Ganesh; John Bernat; Ozlem Goker-Alpan; Kathleen Nicholls; Madeleine V. Pahl; Patrick B. Deegan; Chester B. Whitley; Derralynn Hughes; Liching Cao; Michael Chen; Lisa Shiue; Lisa Rojkjaer; William R. Wilcox