P1357: MILESTONE (MODIFYING ELANE GOLDBERG–HOGNES BOX TO INHIBIT EXPRESSION), A UNIVERSAL, SAFE AND EFFECTIVE CRISPR/CAS9N-MEDIATED GENOME EDITING STRATEGY FOR ELANE RELATED SEVERE CONGENITAL NEUTROPENIA

Posters Diseases of the blood and blood-forming organs RC633-647.5
DOI: 10.1097/01.hs9.0000972316.76856.78 Publication Date: 2023-08-08T16:28:14Z