Establishing Clinical Trial Endpoints in Selecting Patients for RPGR Retinal Gene Therapy
Adult
Male
Clinical Trials as Topic
Endpoint Determination
Patient Selection
Visual Acuity
Genetic Therapy
Retina
Young Adult
Mutation
Humans
Visual Field Tests
Female
Visual Fields
Eye Proteins
Tomography, Optical Coherence
Retinitis Pigmentosa
Retrospective Studies
DOI:
10.1167/tvst.13.9.18
Publication Date:
2024-09-17T16:30:41Z
AUTHORS (4)
ABSTRACT
Clinical trials for X-linked retinitis pigmentosa (RP) often assess retinal structure using optical coherence tomography (OCT) and function microperimetry to evaluate initial eligibility endpoints. Therefore, we seek determine which parameters might be most sensitive in screening new patients enrollment.
SUPPLEMENTAL MATERIAL
Coming soon ....
REFERENCES (41)
CITATIONS (2)
EXTERNAL LINKS
PlumX Metrics
RECOMMENDATIONS
FAIR ASSESSMENT
Coming soon ....
JUPYTER LAB
Coming soon ....