SUNFISH Part 2: Efficacy and Safety of Risdiplam (RG7916) in Patients with Type 2 or Non-Ambulant Type 3 Spinal Muscular Atrophy (SMA) (1260)

• DOI: 10.1212/wnl.94.15_supplement.1260
• Publication Date: 2023-12-07T05:28:50Z
• Authors: Eugenio Mercuri; Nina Barisic; Odile Boespflug-T...; Nicolas Deconinck; Anna Kostera-Prus...; Riccardo Masson; Elena Mazzone; Andres Nascimento; Kayoko Saito; Dmitry Vlodavets; Carole Vuillerot; Sabine Fuerst-Rec...; Sibylle Fuhrer; Marianne Gerber; Ksenija Gorni; Heidemarie Kletzl; Carmen Martin; Wai Yin Yeung; John W. Day