FIREFISH Part 2: Efficacy and Safety of Risdiplam (RG7916) in Infants with Type 1 Spinal Muscular Atrophy (SMA) (1302)

• DOI: 10.1212/wnl.94.15_supplement.1302
• Publication Date: 2023-12-07T05:28:50Z
• Authors: Laurent Servais; Giovanni Baranello; Riccardo Masson; Maria Mazurkiewic...; Kristy Rose; Dmitry Vlodavets; Hui Xiong; Edmar Zanoteli; Muna El-Khairi; Sabine Fuerst-Rec...; Marianne Gerber; Ksenija Gorni; Heidemarie Kletzl; Renata Scalco; Basil T. Darras