Facilitating orphan drug development: Proceedings of the TREAT-NMD International Conference, December 2015, Washington, DC, USA

• DOI: 10.1016/j.nmd.2017.02.013
• Publication Date: 2017-03-05T07:19:17Z
• Authors: E.P. Hoffman; Carsten Bonnemann; Marc Boutin; Bernard Brais; Filippo Buccella; Arthur Burghes; Christopher Coffey; Nabarun Dasgupta; Hugh Dawkins; Annamaria De Luca; Christopher Dowd; Tina Duong; Michelle Eagle; Richard Finkel; Pat Furlong; Cynthia Gagnon; Nathalie Goemans; Michela Guglieri; Yetrib Hathout; Nicholas Johnson; Emil Kakkis; Petra Kaufmann; Jonathan Kimmelman; Lawrence Korngut; Joyce Kullman; Hanns Lochmüller; Stefano Marini; Craig McDonald; Charles Mohan; Lauren Morgenroth; Hiroki Morizono; Kanneboyina Nagaraju; John Porter; Lori Reilly; Markus Rüegg; Joel Schneider; Pietro Spitali; Volker Straub; Lee Sweeney; Giorgio Tasca; Cathy Turner; Olav Veldhuizen; Jan Verschuuren; Susan Ward; Raffaella Willmann
• Keywords: Rigour; Orphan drug; Drug Development; Drug approval

No abstract available