236 SPL84, an antisense oligonucleotide modulating the 3849+10 kb C-T splicing defect, efficiently penetrates and restores CFTR function when treated through the apical side of primary human bronchial epithelial cells

DOI: 10.1016/s1569-1993(23)01166-9 Publication Date: 2023-10-18T06:00:19Z