276 Preclinical and clinical safety profile of SPL84, an antisense oligonucleotide for treatment of people with cystic fibrosis carrying the 3849 +10 Kb C ->T mutation, supporting Phase 2 study initiation

DOI: 10.1016/s1569-1993(24)01116-0 Publication Date: 2024-09-04T09:43:43Z