S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS
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Diseases of the blood and blood-forming organs
RC633-647.5
DOI:
10.1097/01.hs9.0000968000.61396.5e
Publication Date:
2023-08-09T06:01:18Z
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