S272: SAFETY AND EFFICACY OF RM-001 IN PATIENTS WITH TRANSFUSION-DEPENDENT Β-THALASSEMIA: EARLY RESULTS FROM THE ONGOING OF AUTOLOGOUS HBG1/2 PROMOTER-MODIFIED CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS

Oral Sessions Diseases of the blood and blood-forming organs RC633-647.5
DOI: 10.1097/01.hs9.0000968000.61396.5e Publication Date: 2023-08-09T06:01:18Z