A5085019632- Parkinson's Disease Mechanisms and Treatments
- Peripheral Neuropathies and Disorders
- Monoclonal and Polyclonal Antibodies Research
- Hereditary Neurological Disorders
- Statistical Methods in Clinical Trials
- Muscle Physiology and Disorders
- Neurogenetic and Muscular Disorders Research
- Genetic Neurodegenerative Diseases
- Meta-analysis and systematic reviews
- Stroke Rehabilitation and Recovery
- Clinical Reasoning and Diagnostic Skills
- Botulinum Toxin and Related Neurological Disorders
Maastricht University
2021-2023
University of Curaçao
2021
Abstract Background International consensus on IgM ± anti‐MAG PNP (IgM PNP) is lacking. Despite increasing interest in clinical trials, validated disease‐specific measures are needed to adequately capture limitations and changes over time. The IMAGiNe anti‐myelin associated glycoprotein [MAG] peripheral neuropathy) study surges as an international collaboration create a standardized registry of patients with PNP. consortium, which currently consists 11 institutions from 7 countries, presents...
Facioscapulohumeral muscular dystrophy (FHSD) is a debilitating inherited muscle disease for which various therapeutic strategies are being investigated. Thus far, little attention has been given in FSHD to the development of scientifically sound outcome measures fulfilling regulatory authority requirements. The aim this study was design patient-reported Rasch-built interval scale on activity and participation FSHD.
This commentary is on the original article by Vanmechelen et al. pages 683–690 of this issue.