A5010788979- Muscle Physiology and Disorders
- Innovations in Medical Education
- RNA Interference and Gene Delivery
- Clinical Reasoning and Diagnostic Skills
- MicroRNA in disease regulation
- RNA Research and Splicing
- Empathy and Medical Education
- RNA modifications and cancer
- Silk-based biomaterials and applications
University of Illinois Chicago
2024
Illinois College
2024
Nationwide Children's Hospital
2022-2023
Duchenne muscular dystrophy (DMD) is a devastating muscle-wasting disease that arises due to the loss of dystrophin expression, leading progressive motor and cardiorespiratory function. Four exon-skipping approaches using antisense phosphorodiamidate morpholino oligomers (PMOs) have been approved by FDA restore DMD open reading frame, resulting in expression functional but internally deleted protein, patients with single-exon duplications, exon skipping has potential full-length expression....
Suhaiba, Aisha BS; Choubey, Apurva S. MD; Drake, Brett Kerns, James PhD; Gonzalez, Mark H. MD, PhD Author Information